Murillo Bartolome, Alvaro ORCID: https://orcid.org/0000-0001-5470-9347, Alpaugh, Melanie, Peter Durairaj, Ruban Rex, Randall, Emma L., Larin, Meghan, Heraty, Laura, Aston, Alys N., Taylor, Alysha S., Mas Monteys, Alex, Stoberl, Nina, Heuchan, Aeverie E. R., Aeschlimann, Pascale, Fears, Kyle, Landles, Christian, Osborne, Georgina F., Mangin, Antoine, Bhattacharyya, Soumyasree, Metzakopian, Emmanouil, Allen, Nicholas D. ORCID: https://orcid.org/0000-0003-4009-186X, Puymirat, Jack, Bates, Gillian P., Davidson, Beverly L., Cicchetti, Francesca, Lelos, Mariah J. ORCID: https://orcid.org/0000-0001-7102-055X and Dion, Vincent ORCID: https://orcid.org/0000-0003-4953-7637
2026.
Cas9 nickase-mediated contraction of CAG/CTG repeats in vivo is accompanied by improvements in Huntington's disease pathology.
Science Translational Medicine
Item availability restricted.
|