Murillo Bartolome, Alvaro ORCID: https://orcid.org/0000-0001-5470-9347, Alpaugh, Melanie, Peter Durairaj, Ruban Rex, Randall, Emma L., Larin, Meghan, Heraty, Laura, Aston, Alys N., Taylor, Alysha S., Mas Monteys, Alex, Stoberl, Nina, Heuchan, Aeverie E. R., Aeschlimann, Pascale, Fears, Kyle, Landles, Christian, Osborne, Georgina F., Mangin, Antoine, Bhattacharyya, Soumyasree, Metzakopian, Emmanouil, Allen, Nicholas D. ORCID: https://orcid.org/0000-0003-4009-186X, Puymirat, Jack, Bates, Gillian P., Davidson, Beverly L., Cicchetti, Francesca, Lelos, Mariah J. ORCID: https://orcid.org/0000-0001-7102-055X and Dion, Vincent ORCID: https://orcid.org/0000-0003-4953-7637
2026.
Cas9 nickase-mediated contraction of CAG/CTG repeats in vivo is accompanied by improvements in Huntington's disease pathology.
Science Translational Medicine
Item availability restricted. |
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Murillo, Alvaro, Alpaugh, Melanie, Larin, Meghan, Randall, Emma L, Heraty, Laura, Durairaj, Ruban Rex, Aston, Alys N, Taylor, Alysha S, Monteys, Alex Mas, Stöberl, Nina, Heuchan, Aeverie ER, Aeschlimann, Pascale, Bhattacharyya, Soumyasree, Allen, Nicholas D ORCID: https://orcid.org/0000-0003-4009-186X, Puymirat, Jack, Davidson, Beverly L, Cicchetti, Francesca, Lelos, Mariah J ORCID: https://orcid.org/0000-0001-7102-055X and Dion, Vincent ORCID: https://orcid.org/0000-0003-4953-7637
2024.
I001 Cas9 nickase-mediated contraction of CAG repeats in Huntington’s disease.
Journal of Neurology, Neurosurgery and Psychiatry
95
(Suppl)
, pp. A141-A142.
10.1136/jnnp-2024-EHDN.283
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Antwi, Frank D., Awad, Tufaha, Larin, Meghan, Heesom, Kate, Lewis, Phil, Reddell, Paul, Poghosyan, Zaruhi ORCID: https://orcid.org/0000-0003-4966-7618, Dewitt, Sharon ORCID: https://orcid.org/0000-0001-8169-8241, Moseley, Ryan ORCID: https://orcid.org/0000-0002-2812-6735 and Knäuper, Vera ORCID: https://orcid.org/0000-0002-3965-9924
2024.
Tigilanol tiglate-induced changes in secretome profiles alter c-Met phosphorylation and cell surface protein expression in H357 head and neck cancer cells.
Cells
13
(11)
, 982.
10.3390/cells13110982
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Murillo, Alvaro, Larin, Meghan, Randall, Emma L, Taylor, Alysha, Lelos, Mariah ORCID: https://orcid.org/0000-0001-7102-055X and Dion, Vincent ORCID: https://orcid.org/0000-0003-4953-7637
2022.
I05 CRISPR-Cas9 nickase-mediated gene editing to treat Huntington’s disease.
Journal of Neurology, Neurosurgery and Psychiatry
93
(Suppl)
, A86.
10.1136/jnnp-2022-ehdn.231
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